Marianne Carlon


Research Partner

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email Marianne Carlon

Expertise

* Studying cystic fibrosis pathophysiology and cell molecular defects (processing, trafficking, ion channel activity) in cell lines and organoid models
* Assay development for phenotypic drug screens using high content imaging
* Experienced in viral vector technology, including CRISPR-Cas, in organoids, for assay development and as a therapeutic strategy for cystic fibrosis

Relevant Publications

ArAAV-CFTRΔR Rescues the Cystic Fibrosis Phenotype in Human Intestinal Organoids and Cystic Fibrosis Mice
Dragana Vidović, Marianne S. Carlon, Mélanie F. da Cunha, Johanna F. Dekkers, Monika I. Hollenhorst, Marcel J. C. Bijvelds, Anabela S. Ramalho, Chris Van den Haute, Marc Ferrante, Veerle Baekelandt, Hettie M. Janssens, Kris De Boeck, Isabelle Sermet-Gaudelus, Hugo R. de Jonge, Rik Gijsbers, Jeffrey M. Beekman, Aleksander Edelman, Zeger Debyser
Published in American Journal of Respiratory and Critical Care Medicine, September 2015 (see publication in Journal or Research Gate )

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